Gene Therapy

Gene Therapy: Latest CAR-T Therapy for Cancer Signals New Era for Life-Saving Treatments

But these breakthroughs are not going to come cheap.

Cancer

FDA approves 2nd gene therapy targeting non-Hodgkin lymphomas

<b>(CNN) —</b> The US Food and Drug Administration has approved a second gene therapy for cancer, the first to target non-Hodgkin lymphomas.<p>The therapy, Yescarta (axicabtagene ciloleucel), is intended for adult patients with certain types of large B-cell lymphoma after other treatments fail.<p>Non-Hodgkin …

Medicine

Daily briefing: Xi’s power, Google’s Lyft bet and gene therapy

<b>Sign up to receive FirstFT by email here</b><p><i>How well did you keep up with the news this week? Take the FirstFT quiz</i>.<p>President Xi Jinping has used China’s …

China

Nature

NEWS<p>FDA advisers back gene therapy for rare form of blindness<p>Therapy that targets disease-causing mutations could become the first of its kind …

Genetics

University of Chicago to offer newly approved gene therapy for adults with cancer

University of Chicago Medicine will be the first health system in the Chicago area to offer a newly approved gene therapy treatment for adults with cancer.<p>The treatment uses a patient’s own modified cells to fight the most common form of non-Hodgkin lymphoma, which is a blood cancer. The treatment …

Cancer

FDA Approves Gene Therapy to Treat Large B-Cell Lymphoma

It's a futuristic shot that claims to cure cancer in a few weeks for about a third of a million dollars.<p>The second of its kind in the U.S., the Food …

Medicine

Gene therapy helped these children see. Can it transform medicine?

When Caroline Carper was 10 years old she saw rain falling from the skies for the first time. “So I was in grammar class, and it started to pour …

Medicine

Miami's most notorious cop named police captain

In March, City of Miami Police Lt. Javier Ortiz was stripped of his gun, temporarily suspended, and forced to do desk work after a county judge …

U.S. Dept. of Homeland Security

The FDA Just Approved a Second Revolutionary Gene Therapy. A Third Is Probably on the Way

The Food and Drug Administration (FDA) has approved Gilead Science unit Kite Pharma’s groundbreaking cancer gene therapy treatment Yescarta. It’s the …

Cancer

Yescarta, second blood cancer gene therapy, approved by FDA

A gene therapy treatment for some hard-to-treat lymphomas was approved Wednesday by the U.S. Food and Drug Administration.<p>The approval for Yescarta …

Cancer

PBS's Documentary 'The Gene Doctors' Arrives Amid A Gene Therapy Boom

This month, PBS is airing a documentary called <i>The Gene Doctors</i> that spotlights several emerging gene therapies, including Spark Therapeutics’ Luxturna, a treatment for a rare form of blindness that won a unanimous thumbs-up last week from an advisory panel to the FDA. In addition to tracing the …

Genetics

uniQure Announces Hemophilia B Gene Therapy Program To Enter Pivotal Study With FIX-Padua Variant in 2018

<i>~ AMT-060 with the FIX-Padua Modification (AMT-061) Demonstrates Substantial Increase in FIX Activity in Non-human Primates ~</i><p><i>~ Plans to Initiate</i> …

Genetics

Gene therapy for advanced lymphoma gets FDA approval

People with advanced lymphoma now have another type of treatment to consider. The Food and Drug Administration has approved Yescarta, a cell-based gene therapy designed to treat large B-cell lymphoma created by Kite Pharma. It's the second time the FDA has approved a gene therapy for use in the US …

Cancer

Brainstorm Health: Thrive Global Samsung App, Gilead Cancer Gene Therapy, Life After Death

Good morning, Dailies. There is nothing radical about most digital media or technology—at least in the sense that it doesn’t make us do things we …

Genetics

First-of-Its-Kind Gene Therapy Could Treat Blindness

A new treatment that could restore vision to people with a rare form of blindness may soon become the first-of-its-kind gene therapy to be approved …

Medicine

The daily business briefing: October 19, 2017

1.<p>Stock futures fall after Dow's first close above 23,000<p>U.S. stock futures dropped early Thursday, signaling a pullback as tech shares fell after …

Genetics

A cancer treatment that's part of 'a big new field of medicine' just got approved

The FDA just approved another revolutionary cancer treatment.<p>The treatment, called Yescarta, treats a type of blood cancer called aggressive B-cell non-Hodgkin lymphoma.<p>The highly personalized cancer treatment called CAR T-cell therapy (CAR is short for chimeric antigen receptor) is made by Kite …

Cancer

FDA Approves Another Amazing And Costly Cancer-Killing Gene Therapy

In 2010, Josh Feldman was on his honeymoon — a globe-spanning trip that at one point involved swimming with humpback whales — when he noticed a “Garbanzo-sized” lump on the back of his neck. It turned out to be lymphoma, which worsened even as he cycled through treatments: chemotherapy, the …

Cancer

Everything You Need to Know About CRISPR Genome Editing

Imagine being able to cure any genetic disease, prevent bacteria from resisting antibiotics, alter mosquitoes so they can't transmit malaria, prevent …

Genetics

Scientists Zero In on a New Target for Obesity

For the 35 million American adults who are battling obesity, the age-old advice to “improve diet and exercise” often falls short. And surgical …

Medicine

10 Things to Know for Thursday

Your daily look at late-breaking news, upcoming events and the stories that will be talked about Thursday:<p>1. NEW TURMOIL SWIRLS AROUND TRUMP<p>The …

Gord Downie

Your Daily Pharma Scoop: Everybody's Gilead Problem, Halozyme's Further Progress, ZIOPHARM's Gene Therapy

We discuss an excellent article on Gilead: give up, or hold bulldog style?<p>Halozyme extends its PEGPH20 to new solid tumors.<p>ZIOPHARM’s gene therapy …

Stocks

Cascade of Costs Could Push New Gene Therapy Above $1 Million Per Patient

Outrage over the high cost of cancer care has focused on skyrocketing drug prices, including the $475,000 price tag for the country’s first gene …

Health Care

New gene therapy restores vision in patients suffering from inherited blindness

Leber congenital amaurosis is the most common cause of inherited sight loss in young people.<p>The first successful gene therapy for an inherited form …

Medicine

Voyager Therapeutics Announces New Data Presentations At The Congress Of The European Society Of Gene And Cell Therapy

<i>New data with novel AAV gene therapy capsids demonstrate widespread gene transfer to the brain and spinal cord of non-human primates after a single</i> …

Neuroscience

We may soon have our first $1 million drug. Who will pay for it? And how?

Gene therapy has the potential to be a one-shot treatment that could reverse blindness, restore blood-clotting function to hemophiliacs, or even cure …

Pharma

ZIOPHARM commences early-stage study of gene therapy Ad-RTS-hIL-12 in pediatric brain tumors

• The first patient has been dosed in a Phase 1 clinical trial evaluating ZIOPHARM Oncology 's (ZIOP +0.5%) gene therapy Ad-RTS-hIL-12 with veledimex …

Stock Markets

4 Biotech Stocks Worth Buying A Pullback In

The biotech sector has done quite well year to date.<p>Weakness in several big winners of 2017 could be providing a chance to initiate or add to a …

Stocks

Nightstar Therapeutics - Novel Gene Therapy Company And Recent IPO

The lead program NSR-REP1 is targeting choroideremia, an inherited X-linked disorder.<p>The 2018 data release in X-linked retinitis pigmentosa …

Business

Audentes Therapeutics under pressure from downgrades; shares slip 11%

Thinly traded small cap Audentes Therapeutics (BOLD -11.4%) is under modest pressure on the heels of a downgrade to Neutral by Evercore ISI and to …

Business