Gene Therapy

Massachusetts Mom Convinces Scientists to Find Potential Cure for Daughter’s Rare Disease: ‘Anything Is Possible’

Shortly before Talia Duff of Ipswich, Massachusetts, turned 9, her mother noticed that she was losing mobility. Talia, who has Down syndrome, could …

Medicine

3 Things In Biotech You Should Learn Today: June 28, 2017

Advaxis data selected for presentation at ESGO 2017<p>Acceleron finds meaningful improvement in thalassemia<p>Bluebird provides updates of its own in anemia<p>…

Medicine

Brainstorm Health Daily: June 23, 2017

Senate Republicans finally revealed their super-secret healthcare bill yesterday. And while it’s too early to count votes, I’m guessing that it won’t …

Affordable Care Act

Early Data for bluebird bio Gene-Therapy Candidate Show Some Promise | GEN Genetic Engineering & Biotechnology News - Biotech from Bench to Business | GEN

bluebird bio today disclosed its first data, including some promising results, from a pair of clinical studies assessing its LentiGlobin™ gene …

Medicine

New mechanism for genome regulation discovered: Implications for improving gene therapy

Implications for improving gene therapy<p>The mechanisms that separate mixtures of oil and water may also help the organization of a part of our DNA …

Genetics

Firefly gene illuminates ability of optimized CRISPR-Cpf1 to efficiently edit human genome

Scientists on the Florida campus of The Scripps Research Institute (TSRI) have improved a state-of-the-art gene-editing technology to advance the …

Genetics

3 Things In Biotech You Should Learn Today: June 15, 2017

Kura Oncology's lymphoma drug selected for presentation in Europe.<p>An Array BioPharma partner moves an EGFR inhibitor forward in gastric cancer.<p>AveXis …

Cancer

MilliporeSigma Secures First CRISPR Patent in Australia

Life science business of Merck KGaA MilliporeSigma has been awarded its first patent for CRISPR technology, an Australian patent relating to the use …

Patents

Biotech Forum Daily Digest - Spotlight On Applied Genetics Technology

New leadership at the FDA is starting to target the opioid epidemic that has blossomed over the past decade, which has ramifications for the pain …

Stocks

Cancer Cures, Gene Therapy, Pig Transplants, And More: 10 Early-Stage Biotech Startups To Watch

Biotechnology is a broad sector encompassing technologies that take advantage of cellular or biomolecular processes to develop products across …

Genetics

Why doctors’ offices could become obsolete

A man showing early signs of a heart attack — detected by a bot tracking his heart activity from a sensor on his wrist — is picked up by a …

Medical Technology

Fibrocell's gene therapy candidate FCX-013 nabs Rare Pediatric Disease Designation from FDA; shares ahead 9% premarket

Thinly traded nano cap Fibrocell Science (NASDAQ:FCSC) perks up 9% premarket on light volume in response to its announcement that the FDA has granted …

Medicine

Fibrocell's gene therapy candidate FCX-013 nabs Rare Pediatric Disease Designation from FDA; shares ahead 9% premarket

Stock Markets27 minutes ago (Jun 12, 2017 08:46AM ET)<p>Saved. See Saved Items.<p>This article has already been saved in your Saved Items<p>© Reuters. …

Medicine

Gene Therapy: Potential Breakthrough to Cure Allergies

Gene therapy that erases memory of immune cells against allergens could be a potential new therapy for allergies like asthma and pollen allergy.

Medicine

Safety profile of Genetic Tech's AAV-based gene therapy OK in early-stage study of inherited vision loss disorder

Top-line safety data from a Phase 1/2 clinical trial assessing Applied Genetic Technologies' (NASDAQ:AGTC) adeno-associated virus (AAV)-based gene …

Genetics

Safety profile of Genetic Tech's AAV-based gene therapy OK in early-stage study of inherited vision loss disorder

Stock Markets28 minutes ago (Jun 08, 2017 04:38PM ET)<p>Saved. See Saved Items.<p>This article has already been saved in your Saved Items<p>© Reuters. Safety …

Stock Markets

A new study offers a cautionary tale for using the widely hyped gene-editing tool CRISPR on people.

Credit: Ramon Andrade 3DCiencia/Science Photo Library/Getty ImagesThe gene-editing technology known as CRISPR has only been around for five years, …

Genetics

A New Gene Therapy Could Hold the Key to Curing Allergies and Asthma

Erasing Asthma<p>Scientists from the University of Queensland have used gene therapy to turn off the immune response responsible for asthma. The team …

Medicine

A first: All respond to gene therapy in a blood cancer study

CHICAGO (AP) — Doctors are reporting unprecedented success from a new cell and gene therapy for multiple myeloma, a blood cancer that's on the rise. Although it's early and the study is small — 35 people — every patient responded and all but two were in some level of remission within two months.<p>In …

Medicine

Gene therapy to fight blood cancer finds unprecedented success

At a medical conference in Chicago, doctors reported unprecedented success with a new cell and gene therapy for multiple myeloma, a blood cancer.

Cancer

Scientists may be able to trick your genes into turning off allergies, and this could be so awesome

Breaking news: Science has gotten so advanced, we might be able to turn off severe allergies.<p>This means that people with lethal allergies — think …

Medicine

Gene therapy could wipe immune memory and "turn off" severe allergies

Scientists may be one step closer to discovering a way to genetically "turn off" allergic responses with a single injection. A team of researchers at …

Medicine

Scientists just discovered a way to 'turn off' allergies for good

Scientists in Australia claim to have discovered what could be a life-long cure for potentially fatal allergies to peanuts, shellfish and other …

Medicine

Allergy research 'breakthrough' could lead to treatment in a decade, UQ researchers say

Sufferers of severe allergies like asthma and lethal food allergies could gain lifetime relief in a single treatment, with Queensland researchers …

Medicine

From AAV to CRISPR: Era of hacking our bodies is just beginning

In the 1997 film <i>Gattaca</i>, the future society depicted has achieved mainstream genetic modification, so much so that before a child is born, their …

Genetics

Gene Therapy Has Been Used to 'Switch Off' Asthma Symptoms

And it could apply to bee, peanut, and shellfish allergies.<p>Scientists have used gene therapy to 'switch off' the immune response that causes asthma, …

Medicine

Gene therapy could 'turn off' severe allergies

A single treatment giving life-long protection from severe allergies such as asthma could be made possible by recent immunology research.

Medicine

'Overwatch' Hammond: Blizzard might be teasing a new character, Horizon Lunar Colony map

Something new is on the way to <i>Overwatch</i> very soon, and it seems like it could be a new hero named Hammond, a new map on the Horizon Lunar Colony — or …

Activision Blizzard

Spark Therapeutics: Upcoming FDA Catalyst

Spark Therapeutics’ recently applied for an FDA approval for its blindness-related one-time gene therapy treatment.<p>The treatment has a high accuracy …

Stocks

Scientists Use the Tweaked Genes of a Virus to Halt Vision Loss

What if you could tweak the genes of a virus to turn its ability to invade cells into a delivery system for eyesight therapy? That’s what researchers …

Pets